About Gene Therapeutics Research

Gene therapy offers hope for nearly every field of medicine. In the not-too-distant future, diabetes could be prevented before it occurs. Cancers could be controlled or even cured. Alzheimer's and Parkinson's disease could be cured or significantly delayed. A fetus with Tay-Sachs disease could be genetically treated in the womb. The risk of organ transplant rejection could be dramatically reduced. The Gene Therapeutics Research Institute's researchers, in collaboration with clinical researchers, are seeking medical advances in a wide range of clinical disorders, including:

  • Parkinson's and Alzheimer's disease
  • Cancers, including brain tumors and breast cancer
  • Heart disease
  • Organ transplantation
  • Metabolic disorders
  • Intrauterine fetal disorders
  • Diabetes
  • Blood diseases
  • Inflammatory bowel disease
  • Infectious diseases
As one of the few facilities in the western United States capable of this type of research, Cedars-Sinai is in a unique position to help patients benefit directly from genetic research. The Board of Governors Gene Therapeutics Research Institute collaborates with other disciplines at Cedars-Sinai so that gene-based research that proves to be effective can be quickly put into medical practice.